Lysosomal Storage Diseases Infographic
Through comprehensive data analysis, Beacon has identified 175 assets for LSDs, accounting for 8% of our database. Most of these assets are still preclinical and use classical gene therapies. We have observed that adeno-associated viruses (AAV) are the most common delivery systems used, with AAV9 being the second most common serotype leveraged due to its unique targeting capabilities.
Our analysis also revealed that most genes targeted by LSD assets are lysosomal or responsible for breaking down large carbohydrates. Large pharmaceutical companies dominate the developer landscape for LSDs due to the considerable amount of money required to translate research into clinical trials. Join us as we explore the landscape of LSD research and development.
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Learn More About Gene Therapy
- The Most Comprehensive Way to Search the Gene Therapy Development Landscape: Unique search ontologies based on Gene Therapy drug and trial characteristics
- Market Leading Approach to Gene Therapy Preclinical & Clinical Data Curation: Manual curation of key Gene Therapy research and development data points by Gene Therapy research scientists
- Seamlessly Integrate Commercial & Scientific Data all in One Place: Search Gene Therapy company and deal data based on their pipeline and technologies.
- Unrivalled Granularity in Reports & Analysis: Our search ontology and technology indexing enable comprehensive analysis not seen elsewhere.
What is Beacon?
Beacon is the essential intelligence platform for R&D decision-makers working in pharma and biotech, offering unique technology and drug datasets for complex therapeutics and disease areas.
Our market-defining proprietary ontologies, manual data curation, and accurate and comprehensive life science data, provide our customers with unparalleled visibility of the drug, trial and commercial landscape.
This is why 24 of the top 25 pharmaceutical companies trust Beacon to power their critical pipeline, competitive, and commercial decisions.
We’d welcome the opportunity to show you how Beacon can transform your data strategy. Book your personalized demonstration today!
